CAREERS
About Us
SCIENTIFIC FOCUS
Our Focus
Our Platform Technologies:
Turbo-ZM™ RMAs / ERSGs
Class 1 CF
PIPELINE
Pipeline
Class 1 CF
RDEB/JEB
FAP & CRC
Alport Syndrome
Scientific Documents
INVESTORS
Overview
Press Releases
Events & Presentations
Corporate Governance
Financials and Filings
Stock Information
Analyst Coverage
Investment Inquiries
CAREERS
DEEP PIPELINE of
First-in-class therapies
Our
Pipeline
Learn more
about our programs for:
Class 1 cystic fibrosis (CF)
Recessive dystrophic
epidermolysis bullosa (RDEB) /
Junctional epidermolysis bullosa (JEB)
Familial adenomatous
polyposis (FAP) & APC mutant
colorectal cancer (CRC)